Ophthalmology Times

EURETINA 2026: 3 gene therapy programmes for nAMD approaching phase 3 readouts

At EURETINA 2026, Arshad Khanani, MD, FASRS, reviews sura-vec, 4D-150 and ixo-vec, 3 nAMD gene therapies in phase 3 with ...

What’s The Latest On CRISPR Gene Editing Technology?

CRISPR is one of this generation’s most profound innovations, with the potential to fundamentally alter the realm of modern ...

Genezen Partners with Nevena Lešević and University of Missouri to Advance Personalized AAV9 Gene Therapy for Her Son with Ultra-Rare ARCA2

Genezen, a gene therapy contract development and manufacturing organization (CDMO), today announced a partnership with Nevena Lešević of Lazarevac, Serbia to support the manufacturing of an AAV ...

From "Preservation" to "Improvement": A Concept for Remodeling Transplant Lungs via Gene Therapy

Summary of arguments from the Toronto Thoracic Surgery Summit lecture video and implications for business decisionsDate of ...
STAT

Drug meant to make gene therapy safer may also make it less effective

Jason is a general assignment reporter, with particular focus on genetic medicine and rare disease. Confidential tips can be sent on Signal at JasonMast.77. BOSTON — A medicine increasingly used to ...
Ophthalmology Times

Gene therapy 4D-150 enters phase 3 in DME with 4SIGHT trial launch

The first patients have been enrolled in 4SIGHT, a global phase 3 trial comparing a single intravitreal injection of the investigational gene therapy 4D-150 with aflibercept 2 mg ...
Psychiatry Advisor

First Gene Therapy for Sanfilippo Syndrome Type A Gets FDA Approval

FDA approves Fayuvi (rebisufligene etisparvovec-hopf), the first gene therapy for pediatric patients with mucopolysaccharidosis type IIIA (MPS IIIA).

Beacon's gene therapy for vision loss condition meets main trial goal

Sept 21 (Reuters) - Beacon Therapeutics said on Monday its experimental gene therapy improved the ability to read in low-light conditions in a late-stage trial on people with a form of inherited eye ...

Cell And Gene Therapy Has Advanced: Can Healthcare Systems Keep Up?

Realizing the potential of cell and gene therapies will require organizations to rethink how they finance care and build the ...
BioSpace

Ray Therapeutics Awarded $8 Million CIRM Grant to Advance RTx-021 Gene Therapy for Stargardt Disease

Ray Therapeutics (RayTx), an industry-leading clinical-stage biopharmaceutical company pioneering differentiated vision ...

Gene therapy: The breakthrough that inspired Spider-Man | Euronews Tech Talks

Although an inspiration for science fiction movies, gene therapy is real. Here is how it works and what could be improved ...

South Korea Cell and Gene Therapy Manufacturing Market Forecast to 2035 | 29.56% CAGR Unlocks a USD 7.54 Billion Opportunity in CDMO Capacity and GMP Expansion

Capitalize on GMP-certified CDMOs, regulatory fast tracks and key bio-clusters; prioritize contract manufacturing, commercial scale-up and gene therapy capabilities.Dublin, Oct. 01, 2026 (GLOBE ...